What you'll learn

  • Learn the fundamental concepts of gene therapy including the different modalities,

    critical terminology, and necessary components

  • Gain an understanding of the key differences between ex vivo and in vivo gene

    therapies, including their unique uses, delivery methods, and challenges

  • See how ex vivo and in vivo gene therapies can be clinically applied to treat

    inherited genetic conditions

Course description

With all the advances in science and with closer collaboration between different scientific disciplines, gene therapy has become a promising treatment option for some genetic conditions and is being heavily investigated for many others. Therefore, learning about gene therapy and how it’s done has important implications for anyone working in health care and related sectors.

This advanced course offers a unique way for professionals to learn from leading Harvard Medical School faculty about gene therapy and about the advances happening in this field that are ultimately helping to improve the treatment of certain genetic diseases.